Brogidirsen shows motor benefits and safety over 3.5 years of treatment in people with DMD who are amenable to exon 44 ...

Three boys with DMD given the gene therapy GNT0004 in a trial showed sustained improvements in motor function after two years ...

Feeling discouraged by the progression of his FSHD, columnist Robin Stemple focuses on the love and kind gestures he's ...

Columnist Shalom Lim and his girlfriend, Amanda, were among the disability advocates who let their voices be heard at a ...

By grounding himself in the reasons why he keeps moving forward, columnist Patrick Moeschen is able to figure out how to ...

Avidity's exon-skipping therapy del-zota led to functional gains for people with DMD, regardless of their walking abilities, ...

Columnist Betty Vertin's sons with Duchenne MD have seen their social circle shrink over the years, but they now enjoy time with each other.

Health Canada has approved Agamree (vamorolone) to treat Duchenne muscular dystrophy (DMD) in patients ages 4 and older, making Agamree the first approved DMD treatment in Canada. DMD is caused by ...

Yeah, when you’re having a caregiver or individual helping you out, overstepping and you want to set boundaries, the best way to communicate that is really just to communicate it — to tell them in ...