Bioengineers at Rice University have developed a nonsurgical method to control seizure-related brain activity using sound ...

Type 1 diabetes is an autoimmune disease in which the insulin-producing β cells in the pancreatic islets of Langerhans are ...

Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

In a world-first trial, scientists used a one-off CRISPR gene edit to switch off a liver “fat brake” gene, slashing stubborn ...

One dose of an experimental drug cover offer lifetime treatment for people with high cholesterol, but its long-term safety is ...

A new gene-editing technique enables the correction of multiple genetic mutations simultaneously, transforming the prospects ...

Q3 2025 Earnings Call Transcript November 4, 2025 Taysha Gene Therapies, Inc. misses on earnings expectations. Reported EPS ...

Over the past two decades, synthetic biology has fueled advancements across a broad range of disciplines, including agriculture, bioremediation, biofuel production, and chemical manufacturing. Today, ...

For years, cell and gene therapies were mainly associated with rare and orphan diseases, those that impact small patient groups and lack effective treatment options. However, recent developments in ...

A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated children, offering a lasting, donor-free solution to ADA-SCID, known as the ...

A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on her own, two years after the treatment. Opal Sandy made history in 2023 when at 11 ...