Personalized vitamin D supplementation -- often requiring 5,000 IU of vitamin D each day -- did prove to have secondary ...

MeiraGTx Holdings has signed a deal with Eli Lilly , potentially worth over $475 million, granting the pharma giant rights to ...

A CRISPR-based gene therapy showed improvement in lipids in difficult-to-treat patients, but one study raised flags after a ...

A single infusion of CRISPR Therapeutics' experimental gene therapy was safe and reduced levels of harmful LDL cholesterol ...

Preclinical data with a gene therapy has shown potential to restore cardiac function in a rat model of for heart failure.

NEW ORLEANS – A single injection of a gene-edited protein was deemed productive and safe in patients with dyslipidemia that ...

Researchers report early but encouraging results on an experimental gene-editing treatment for high cholesterol.

Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

This report, published by Towards Healthcare, a sister firm of Precedence Research, provides an in-depth analysis of the ...

MeiraGTx’s AAV-AIPL1 has already led to vision gains in blind children, as regulatory submissions for the gene therapy close ...

These findings highlight the potential of self-complementary AAVs to reduce dose requirements, minimize toxicity, and broaden ...

In a world-first trial, scientists used a one-off CRISPR gene edit to switch off a liver “fat brake” gene, slashing stubborn ...