Nearly all children with spinal muscular atrophy who started on Evrysdi before symptom onset are walking after three years, ...

Columnist Helen Baldwin worried the baby who arrived May 18, 1997, would keep everyone awake, but his silence signaled a ...

SMA Europe has launched an online tool designed to help patients, doctors, and others in the spinal muscular atrophy (SMA) ...

The exergame Tales from the Magic Keep aims to boost physical activity, and proved to be a feasible tool for children with ...

The apitegromab approval process reminded guest writer Joanna Buoniconti of lessons about keeping hope alive while protecting ...

For people with spinal muscular atrophy, physical therapy can help support mobility, strength, and quality of life, regardless of SMA type.

The 2023 film “American Fiction” follows a frustrated writer named Thelonious “Monk” Ellison (portrayed by Jeffrey Wright). While his books receive critical praise, his lack of commercial success ...

“Come on, girl, just use your four extra arms!” I often tease my friends like this when we’re trying to accomplish a tricky caregiving task together. Some things would go a lot smoother if we had more ...

The U.S. Food and Drug Administration (FDA) has declined to approve apitegromab as a treatment for spinal muscular atrophy (SMA). The FDA said it could not approve developer Scholar Rock‘s application ...

There is currently no cure for spinal muscular atrophy (SMA) yet, but there are a number of treatments that can delay the progression of symptoms, as well as several experimental treatments currently ...

For adults with spinal muscular atrophy (SMA), a genetic disease that progressively weakens breathing muscles, the approved treatment Spinraza (nusinersen) offers a crucial long-term benefit — stable ...